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Functional rescue of F508del-CFTR through revertant mutations introduced by CRISPR base editing
Irene Carrozzo
•
Giulia Maule
•
Carmelo Gentile
altro
Anna Cereseto
2024
journal article
Periodico
MOLECULAR THERAPY
DOI
10.1101/2024.08.28.610115
Archivio
https://hdl.handle.net/11390/1317206
info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85218855641
Diritti
metadata only access
google-scholar
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